P.27Targeted delivery of oligonucleotide therapeutics to muscle reduces toxic DMPK RNA

Mohammed Qatanani(Scholar Rock (United States)), Raju Subramanian, Sean Spring(Abeona Therapeutics (United States)), Nelson Hsia, Ming Yao(Karolinska University Hospital), Timothy Weeden, C. Stehman-Breen, Canada Desjardins, Bernadette Connolly(University of Aberdeen)
Neuromuscular Disorders
September 29, 2019
Cited by 0


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