Role of Regulatory T Cell and Effector T Cell Exhaustion in Liver-Mediated Transgene Tolerance in Muscle

Jérôme Poupiot(Inserm), Giuseppe Ronzitti(Inserm), Romain Hardet(Inserm), Fanny Collaud(Inserm), Laurent Bartolo(University of Pennsylvania), Pasqualina Colella(Stanford Medicine), Peggy Sanatine(Genethon (France)), Jean Davoust(Baylor University Medical Center), Federico Mingozzi(Spark Therapeutics (United States)), Helena Costa Verdera(Spark Therapeutics (United States))
Molecular Therapy — Methods & Clinical Development
September 3, 2019
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