Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction
Keiichiro Suzuki(Salk Institute for Biological Studies), Juan Carlos Izpisúa Belmonte(Salk Institute for Biological Studies)
Cited by 67
Related Papers
Disease-corrected haematopoietic progenitors from Fanconi anaemia induced pluripotent stem cells
|Nature|2009|692
Use of the CRISPR/Cas9 system as an intracellular defense against HIV-1 infection in human cells
|Nature Communications|2015|335
Modelling Fanconi anemia pathogenesis and therapeutics using integration-free patient-derived iPSCs
|Nature Communications|2014|117