Effectiveness and safety of the tri-iodothyronine analogue Triac in children and adults with MCT8 deficiency: an international, single-arm, open-label, phase 2 trial
Stefan Groeneweg(Erasmus University Rotterdam), W. Edward Visser(Erasmus MC), Athanasia Stoupa(Hôpital Necker-Enfants Malades), Jan Lebl(Charles University), P Vrijmoeth, Dana Craiu, Yogen Singh(University of Cambridge), Nicole I. Wolf(Emma Kinderziekenhuis), Adri van der Walt(Cape Town Science Centre), Marco Medici(Radboud University Nijmegen), Sylvia Depoorter(AZ Sint-Jan), Davide Tonduti, Federica Zibordi(Fondazione IRCCS Istituto Neurologico Carlo Besta), Marco Cappa(Bambino Gesù Children's Hospital), Krishna Chatterjee(University of Cambridge), Angelique Zandstra, Roelineke J. Lunsing(University Medical Center Groningen), Corstiaan A. den Uil(Maasstad Ziekenhuis), Anne McGowan(University of Cambridge), Yolanda B. de Rijke(Erasmus University Rotterdam), S Nowak(Refaja Ziekenhuis), Klára Roženková(Charles University), Isabelle Petit(Université Fédérale de Toulouse Midi-Pyrénées), Enrico Bertini(Bambino Gesù Children's Hospital), Femke K. Aarsen(Princess Máxima Center), Robin P. Peeters(Unknown), Linda De Meırleır(Vrije Universiteit Brussel), M. Carola Zillikens(Erasmus MC), Diana Bârcă(Clinical Emergency Hospital Bucharest), Martien Manshande('s Heeren Loo), Heiko Krude(Humboldt-Universität zu Berlin), Michel Polak(Hôpital Necker-Enfants Malades), I.F.M. de Coo(Maastricht University), Carla Moran(University College Dublin), Frank E. Visser('s Heeren Loo), Marieke M van der Knoop(Erasmus MC), Ingrid M. van Beynum(Erasmus MC - Sophia Children’s Hospital), Marie‐Claire Y. de Wit(Erasmus MC), Laura Paone(Bambino Gesù Children's Hospital), Jurgen Jansen(Meander Medisch Centrum), Theo J. Visser(Erasmus MC), Jana Malíková(Charles University), Greta Lyons(University of Cambridge), Gautam Ambegaonkar(Cambridge University Hospitals NHS Foundation Trust), Françoise Auriol(Université Fédérale de Toulouse Midi-Pyrénées), Alice Dica(Spitalul Clinic de Psihiatrie Alexandru Obregia)
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