Clinical burden of illness in patients with phenylketonuria (PKU) and associated comorbidities - a retrospective study of German health insurance claims data

K. F. Trefz(Heidelberg University), Frank Rutsch(Klinik und Poliklinik für Kinder- und Jugendmedizin), Ania C. Muntau(University Medical Center Hamburg-Eppendorf), Manu Jain(Northwestern University), Ashok Kumar Jha(BioMarin (United Kingdom)), Sebastian Braun(Goethe University Frankfurt), Carmen Schröder, KM Kohlscheen, Paul Lane(BioMarin (United Kingdom)), Christian Jacob, Wolfgang Greiner(Bielefeld University), Ignacio Alvarez(BioMarin (United Kingdom)), J. Altevers
Orphanet Journal of Rare Diseases
July 22, 2019
10.1186/s13023-019-1153-y
Cited by 96

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