Gene Therapy Corrects Brain and Behavioral Pathologies in CLN6-Batten Disease

Jacob T. Cain(Sanford Research), Shibi Likhite(Nationwide Children's Hospital), Katherine A. White(Sanford Research), Derek Timm(Sanford Research), Samantha S. Davis(Sanford Research), Tyler B. Johnson(Sanford Research), Cassandra Dennys-Rivers(Nationwide Children's Hospital), Federica Rinaldi(Nationwide Children's Hospital), Dario Motti(Nationwide Children's Hospital), Sarah Corcoran(Nationwide Children's Hospital), Pablo Morales, Christopher R. Pierson(Nationwide Children's Hospital), Stephanie M. Hughes(University of Otago), Stella Y. Lee(Kansas State University), Brian K. Kaspar(Baxalta (United States)), Kathrin Meyer(Nationwide Children's Hospital), Jill M. Weimer(University of South Dakota)
Molecular Therapy
July 10, 2019
Cited by 58Open Access
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