Inotersen for the treatment of adults with polyneuropathy caused by hereditary transthyretin-mediated amyloidosis

Morie A. Gertz(Medical University of South Carolina), Laura Obici(University of Pavia), Chafic Karam(Amyloidosis Foundation), Carol Whelan(The Royal Free Hospital), Brian Drachman(Penn Presbyterian Medical Center), Morton Scheinberg(Université Paris-Sud), Stephen B. Heitner(Brigham and Women's Hospital), Sami Khella(University of Lisbon), Márcia Waddington‐Cruz(Université Paris-Sud)
Expert Review of Clinical Pharmacology
July 3, 2019
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