Developing ABEmax-NG with Precise Targeting and Expanded Editing Scope to Model Pathogenic Splice Site Mutations In Vivo

Shisheng Huang(ShanghaiTech University), Xingxu Huang(Chinese National Human Genome Center), Zongyang Lu(ShanghaiTech University), Guanglei Li(Fuwai Yunnan Cardiovascular Hospital), Zhaodi Liao(Chinese Academy of Sciences), Xiajun Li(Harvard University), Zhen Liu(Peking University), Yu Zhang(Chinese National Human Genome Center), Jianan Li(General Hospital of Shenyang Military Region), Xu Ma(National Health and Family Planning Commission), Qiang Sun(Chinese Academy of Sciences), Xiangyang Li(ShanghaiTech University)
iScience
May 1, 2019
Cited by 34


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