Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy
Christopher E. Nelson(Duke University), Yaoying Wu(Duke University), Matthew Gemberling(Duke University), Matthew L. Oliver(Duke University), Matthew A. Waller(Duke University), Joel D. Bohning(Duke University), Jacqueline N. Robinson-Hamm(Duke University), Karen Bulaklak(Duke University), Ruth M. Castellanos Rivera(University of North Carolina at Chapel Hill), Joel H. Collier(Duke University), Aravind Asokan(Duke Medical Center), Charles A. Gersbach(Duke University)
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