Efficacy and safety of burosumab in children aged 1–4 years with X-linked hypophosphataemia: a multicentre, open-label, phase 2 trial

Michael P. Whyte(Shriners Hospitals for Children - St. Louis), Erik A. Imel(Indiana University – Purdue University Indianapolis), Alison Skrinar, Thomas O. Carpenter(Yale University), Gary S. Gottesman(Shriners Hospitals for Children - St. Louis), Javier San Martín(Universidad Nacional de Educación a Distancia), Meng Mao(Guiyang Medical University)
The Lancet Diabetes & Endocrinology
January 9, 2019
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