Development of a gene-editing approach to restore vision loss in Leber congenital amaurosis type 10

Morgan L. Maeder(Editas Medicine (United States)), Haiyan Jiang(Inner Mongolia Agricultural University), Abhishek Dass(Editas Medicine (United States)), Gregory Gotta(Editas Medicine (United States)), Tongyao Wang(Editas Medicine (United States)), Eugenio Marco(Editas Medicine (United States)), George S. Bounoutas(Editas Medicine (United States)), Vidya Dhanapal(Editas Medicine (United States)), Deepak Reyon(Harvard University), Georgia Giannoukos(Editas Medicine (United States)), David Bumcrot(Editas Medicine (United States)), Steven J. Samuelsson(Procter & Gamble (United States)), Terence Ta(Editas Medicine (United States)), Hoson Chao(Editas Medicine (United States)), Scott Haskett(Editas Medicine (United States)), Hariharan Jayaram(Editas Medicine (United States)), Diana Tabbaa(Broad Institute), Michael Stefanidakis(Editas Medicine (United States)), Pam Stetkiewicz(Editas Medicine (United States)), Tim Fennell(Broad Institute), Christopher J. Wilson, Luis Barrera(Beam Therapeutics (United States)), Sebastian Gloskowski(Editas Medicine (United States)), Maxwell N. Skor(Editas Medicine (United States)), Shivangi Joshi(Editas Medicine (United States)), Joy E. Horng(Massachusetts General Hospital), Reshica Baral(Editas Medicine (United States)), Alexandra Glucksmann(Editas Medicine (United States)), Vic E. Myer, Clifford Yudkoff(Editas Medicine (United States)), Charles F. Albright(Editas Medicine (United States)), Rina J. Mepani(Editas Medicine (United States)), Bei Hopkins, Dawn Ciulla(Broad Institute), Jennifer A. DaSilva(Editas Medicine (United States)), Shen Shen(Capital Medical University), Ari E. Friedland
Nature Medicine
January 21, 2019
Cited by 708


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