Efficacy of Ruxolitinib Therapy in a Patient With Severe Enterocolitis Associated With a STAT3 Gain-of-Function Mutation
Marianna Parlato(Université Paris Cité), Georgia Malamut(Délégation Paris 5), Bernadette Bègue(Délégation Paris 5), Elie Abi Nader(Hôpital Necker-Enfants Malades), Julie Bruneau(Délégation Paris 5), Shérine Khater(Hôpital Européen Georges-Pompidou), Christophe Cellier(Assistance Publique – Hôpitaux de Paris), Matthieu Allez(Inserm), Capucine Pïcard(Délégation Paris 5), Olivier Hermine(Centre National de la Recherche Scientifique), Fabienne Charbit‐Henrion(Hôpital Necker-Enfants Malades), Elizabeth Macintyre(Inserm), Olivier Goulet(Hôpital Necker-Enfants Malades), Nicolas Guégan(Délégation Paris 5), Rieux-Laucat Frédéric(Délégation Paris 5), Lionel Le Bourhis(Inserm), Nadine Cerf–Bensussan(Université Paris Cité)
Cited by 42
Related Papers
<i>LMO2</i> -Associated Clonal T Cell Proliferation in Two Patients after Gene Therapy for SCID-X1
|Science|2003|3.5k
International Consensus Classification of Myeloid Neoplasms and Acute Leukemias: integrating morphologic, clinical, and genomic data
|Blood|2022|2.8k
Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1
|Journal of Clinical Investigation|2008|1.8k