A limb-girdle muscular dystrophy 2I model of muscular dystrophy identifies corrective drug compounds for dystroglycanopathies
Peter R. Serafini(Boston Children's Hospital), Matthew S. Alexander(Boston Children's Hospital), Jeffrey J. Widrick(University of Massachusetts Chan Medical School), Rylie M. Hightower(Children's of Alabama), Genri Kawahara(Boston Children's Hospital), Corinne E. Augelli‐Szafran(Southern Research Institute), Louis M. Kunkel(Boston Children's Hospital), Omar Moukha‐Chafiq(Southern Research Institute), Angela Lek(Muscular Dystrophy Association), Daniela Garcia-Perez(Children's of Alabama), Devin Gibbs(Boston Children's Hospital), Natássia M. Vieira(Boston Children's Hospital), Michael Feyder(Boston Children's Hospital)
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