Pompe Disease: From Basic Science to TherapyLara J. Kohler(National Institutes of Health), Nina Raben(National Institutes of Health)NeurotherapeuticsAugust 16, 201810.1007/s13311-018-0655-yCited by 230SaveCiteExport RISWatch citationsRelated PapersTranscription factor EB (TFEB) is a new therapeutic target for Pompe disease|EMBO Molecular Medicine|2013|337Fiber Type Conversion by PGC-1α Activates Lysosomal and Autophagosomal Biogenesis in Both Unaffected and Pompe Skeletal Muscle|PLoS ONE|2010|61