The fragile X mutation impairs homeostatic plasticity in human neurons by blocking synaptic retinoic acid signaling

Zhenjie Zhang(Stanford Medicine), Samuele Marro(California Institute for Regenerative Medicine), Yingsha Zhang(Stanford University), Kristin L. Arendt(Stanford Medicine), Christopher Patzke(Stanford University), Bo Zhou(Stanford University), Tyler Fair(California Institute for Regenerative Medicine), Nan Yang(California Institute for Regenerative Medicine), Thomas C. Südhof(Howard Hughes Medical Institute), Marius Wernig(California Institute for Regenerative Medicine), Lu Chen(Stanford Medicine)
Science Translational Medicine
August 1, 2018
Cited by 121

Abstract

mutations that might contribute to neuronal dysfunction in FXS. In addition, our results suggest that FXS patient iPS cell-derived neurons might be useful for studying the mechanisms mediating functional abnormalities in FXS.


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