Short-term safety of mTOR inhibitors in infants and very young children with tuberous sclerosis complex (TSC): Multicentre clinical experience

Darcy A. Krueger(Cincinnati Children's Hospital Medical Center), David Neal Franz(Cincinnati Children's Hospital Medical Center), Sergiusz Jóźwiak(Children's Memorial Health Institute), Petrus de Vries, Federico Ramos(Hospital Sant Joan de Déu Barcelona), Anna Jansen(Vrije Universiteit Brussel), Mary Kay Koenig, David Mowat(UNSW Sydney), John A. Lawson(Universities UK), Kevin C. Ess(Children's Hospital Colorado), Vinodh Narayanan(Translational Genomics Research Institute), Michael Wong(Washington University in St. Louis), Stephanie Bruns(Cincinnati Children's Hospital Medical Center), Michal Tzadok(Edmond and Lily Safra Children's Hospital), Orrin Devinsky(New York University), Paolo Curatolo(University of Rome Tor Vergata), Jamie K. Capal(Cincinnati Children's Hospital Medical Center)
European Journal of Paediatric Neurology
July 3, 2018
Cited by 81


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