Neural stem cells for disease modeling and evaluation of therapeutics for infantile (CLN1/PPT1) and late infantile (CLN2/TPP1) neuronal ceroid lipofuscinoses

Ni Sima(Women's Hospital, School of Medicine, Zhejiang University), Wei Zheng(National Center for Advancing Translational Sciences)
Orphanet Journal of Rare Diseases
April 10, 2018
Cited by 42


Related Papers