The effect of enzyme replacement therapy on clinical outcomes in male patients with Fabry disease: A systematic literature review by a European panel of experts

Dominique P. Germain(Assistance Publique – Hôpitaux de Paris), Marco Spada(University of Turin), Ilkka Kantola(Turku University Hospital), João Paulo Oliveira(Universidade do Porto), Albina Nowak(University of Zurich), Miguel Viana‐Baptista, Bruno Falissard(Inserm), Christoph Wanner(Universitätsklinikum Würzburg), В. В. Фомин(Sechenov University), Max J. Hilz(Friedrich-Alexander-Universität Erlangen-Nürnberg), Mehdi Namdar(Vrije Universiteit Brussel), Ana Jovanović(Manchester Academic Health Science Centre), Aleš Linhart(Charles University), Renzo Mignani(Ospedale Infermi di Rimini), Maurizio Pieroni(Ospedale San Donato), Perry Elliott(St Bartholomew's Hospital)
Molecular Genetics and Metabolism Reports
February 10, 2019
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