An immune tolerance approach using methotrexate in the naïve setting of patients treated with a therapeutic protein: Experience in infantile Pompe disease
Ankit K. Desai(Duke Medical Center), Priya S. Kishnani(Duke Medical Center), D D Niyazov, Pranoot Tanpaiboon(Children's National), Seymour Packman(University of California, San Francisco), Jean‐Marc Nuoffer(University Children’s Hospital Bern), Neerja Gupta(All India Institute of Medical Sciences), Sheela Nampoothiri(Amrita Institute of Medical Sciences and Research Centre), William B. Rizzo, Angelika Erwin(Cleveland Clinic), Alexandra Joseph(Sanofi (United States)), Bradley Troxler(University of Alabama at Birmingham), Sherry Langston(Ochsner Health System), Clarisa Maxit(Hospital Italiano de Buenos Aires), Zoheb B. Kazi(Duke Medical Center), Alison McVie‐Wylie, Crystal Sung, James Weisfield-Adams(University of Colorado Denver), Omar Abdul‐Rahman(Cornell University), Annette Feigenbaum(Hospital for Sick Children), Susan Richards(MRC Clinical Trials Unit at UCL), David Kronn(New York Medical College), M.G. Sabbadini(IRCCS Ospedale San Raffaele), Diana Ballhausen(University of Lausanne), Katalin Scherer(University of Arizona), Marianne Rohrbach(Ghent University Hospital)
Cited by 1
Related Papers
The 2017 international classification of the Ehlers–Danlos syndromes
|American Journal of Medical Genetics Part C Seminars in Medical Genetics|2017|1.9k
Isolation of a candidate gene for Menkes disease and evidence that it encodes a copper–transporting ATPase
|Nature Genetics|1993|1.4k
Outcome of 609 adults after relapse of acute lymphoblastic leukemia (ALL); an MRC UKALL12/ECOG 2993 study
|Blood|2006|843
Proposed guidelines for the diagnosis and management of methylmalonic and propionic acidemia
|Orphanet Journal of Rare Diseases|2014|713