CRISPR/Cas9 Mediated Disruption of the Swedish APP Allele as a Therapeutic Approach for Early-Onset Alzheimer’s Disease

Bence György(University of Basel), Martin Ingelsson(Uppsala University), Lars Lannfelt(BioArctic Neuroscience (Sweden)), Vilmantas Giedraitis(Uppsala University), Dakai Mu(Harvard University), Mikołaj Piotr Zaborowski(Poznan University of Medical Sciences), Benjamin P. Kleinstiver(Harvard University), J. Keith Joung(Massachusetts General Hospital), Ksenia V. Kastanenka(Harvard University), Casey A. Maguire(Harvard University), Bradley T. Hyman(Harvard University), Adrienn Volak(Massachusetts General Hospital), Camilla Lööv(Uppsala University), Caitlin Commins(Harvard University), Xandra O. Breakefield(Harvard University), Shuko Takeda(Osaka Gakuin University)
Molecular Therapy — Nucleic Acids
March 18, 2018
Cited by 189


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