A Universal Approach to Correct Various <i>HBB</i> Gene Mutations in Human Stem Cells for Gene Therapy of Beta-Thalassemia and Sickle Cell Disease

Liuhong Cai(University of Maryland, Baltimore), Linzhao Cheng(University of Maryland, Baltimore)

Stem Cells Translational Medicine

November 21, 2017

10.1002/sctm.17-0066

Cited by 128

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