Strategy to detect pre-existing immunity to AAV gene therapyLillian Falese(BioMarin (United States)), Sylvia Fong(BioMarin (United States))Gene TherapyNovember 6, 201710.1038/gt.2017.95Cited by 98SaveCiteExport RISWatch citationsRelated PapersInterindividual variability in transgene mRNA and protein production following adeno-associated virus gene therapy for hemophilia A|Nature Medicine|2022|112