SGT-001 Micro-dystrophin gene therapy for Duchenne muscular dystrophy

Joel Schneider(Solidus Biosciences (United States)), Carl Morris(Sylvana Research), Diane Golebiowski(University of Massachusetts Chan Medical School), Jorge González(Solidus Biosciences (United States)), Valeria Ricotti(Solidus Biosciences (United States)), Kristy J. Brown(Children's National), Jorge A. Quiroz(Solidus Biosciences (United States))
Neuromuscular Disorders
September 12, 2017
Cited by 20


Related Papers