Elimination of Toxic Microsatellite Repeat Expansion RNA by RNA-Targeting Cas9

Ranjan Batra(University of California San Diego), David A. Nelles(University of California San Diego), Elaine Pirie(University of California San Diego), Steven M. Blue(University of California San Diego), Ryan J. Marina(University of California San Diego), Harrison Wang(University of California San Diego), Isaac A. Chaim(University of California San Diego), James D. Thomas(University of Florida), Nigel Zhang(University of California San Diego), Vu Nguyen(University of California San Diego), Stefan Aigner(University of California San Diego), Sebastian Markmiller(University of California San Diego), Guangbin Xia(University of Florida), Kevin D. Corbett(University of California San Diego), Maurice S. Swanson(University of Florida), G Yeo(Agency for Science, Technology and Research)
Cell
August 1, 2017
Cited by 256Open Access
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