Assessing mNIS+7<sub>Ionis</sub> and international neurologists' proficiency in a familial amyloidotic polyneuropathy trial
William J. Litchy(Mayo Clinic), Marcus Vinícius Pinto(Mayo Clinic in Arizona), Andrea Cortese(University of Pavia), Stephen B. Heitner(Brigham and Women's Hospital), Morie A. Gertz(Medical University of South Carolina), Peter D. Gorevic(Université Paris-Sud), John L. Berk(Boston University), Márcia Waddington‐Cruz(Université Paris-Sud), Rickey E. Carter(Mayo Clinic in Florida), Janice F. Wiesman(Boston University), Annabel K. Wang(Université Paris-Sud), Michelle L. Mauermann(Anna Needs Neuroblastoma Answers), R Bergemann(Mayo Clinic), Violaine Planté‐Bordeneuve(Université Paris-Est Créteil), Katherine Ruzhansky(Medical University of South Carolina), Matilde Laurá(National Hospital for Neurology and Neurosurgery), Namita Goyal(University of California, Irvine), Vinay Chaudhry(Utah Tech University), Karen A. Lodermeier(Mayo Clinic), Samar S. Ayache(Université Paris-Est Créteil), Carol Whelan(The Royal Free Hospital), Thomas H. Brannagan(Columbia University), Isabel Conceição(Université Paris-Sud), Hayet Salhi(Inserm), Brian Drachman(Penn Presbyterian Medical Center), Julie Khoury(Oregon Health & Science University), Steven G. Hughes(Ionis Pharmaceuticals (United States)), Jessica Robinson‐Papp(Icahn School of Medicine at Mount Sinai), Christopher J. Klein(Mayo Clinic), Márcio Cardoso(Centro Hospitalar Lisboa Norte), Michael Polydefkis(Université Paris-Sud), Céline Labeyrie(Bicêtre Hospital), Giampaolo Merlini(University of Pavia), Sami Khella(University of Lisbon), Christina Alves(Biogen (United States)), David Adams(Mount Sinai Health System), Teresa Coelho(Universidade do Porto), João Ferreira(Iscte – Instituto Universitário de Lisboa), Jenny L. Davies(Mayo Clinic), Elizabeth J. Ackermann(Université Paris-Sud), Merrill D. Benson(Indiana University School of Medicine), P. James B. Dyck(Mayo Clinic), John C. Kincaid(Indiana University Health)
Cited by 56
Related Papers
Transcatheter Aortic-Valve Replacement with a Self-Expanding Valve in Low-Risk Patients
|New England Journal of Medicine|2019|3.6k
Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis
|New England Journal of Medicine|2018|2.9k
Tafamidis Treatment for Patients with Transthyretin Amyloid Cardiomyopathy
|New England Journal of Medicine|2018|2.8k
International uniform response criteria for multiple myeloma
|Leukemia|2006|2.6k
Evidence-based guidelines on the therapeutic use of repetitive transcranial magnetic stimulation (rTMS)
|Clinical Neurophysiology|2014|2.2k