Long term survival and cardiopulmonary outcome in children with Hurler syndrome after haematopoietic stem cell transplantation
Su Han Lum(Royal Manchester Children's Hospital), Robert Wynn(Royal Manchester Children's Hospital), Arunabha Ghosh(St Mary's Hospital), Alexander Broomfield(St Mary's Hospital), Simon Jones(Manchester Academic Health Science Centre), Karolina M. Stępień(Medical University of Warsaw), Heather J. Church(St Mary's Hospital), Jean Mercer(St Mary's Hospital)
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