Long term survival and cardiopulmonary outcome in children with Hurler syndrome after haematopoietic stem cell transplantation
Su Han Lum(Royal Manchester Children's Hospital), Robert Wynn(Royal Manchester Children's Hospital), Arunabha Ghosh(St Mary's Hospital), Alexander Broomfield(St Mary's Hospital), Simon Jones(Manchester University NHS Foundation Trust), Karolina M. Stępień(Salford Royal NHS Foundation Trust), Heather J. Church(St Mary's Hospital), Jean Mercer(St Mary's Hospital)
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