Characterizing the effect of GalNAc and phosphorothioate backbone on binding of antisense oligonucleotides to the asialoglycoprotein receptor
Karsten Schmidt(Ionis Pharmaceuticals (United States)), Punit P. Seth(Ionis Pharmaceuticals (United States)), Eric E. Swayze(Ionis Pharmaceuticals (United States)), Hans Gaus(Ionis Pharmaceuticals (United States)), Michael E. Østergaard(Ionis Pharmaceuticals (United States)), Garth A. Kinberger(Ionis Pharmaceuticals (United States)), Aaron J. Donner(University of Colorado Boulder), Thazha P. Prakash(Ionis Pharmaceuticals (United States)), Audrey Low(Ionis Pharmaceuticals (United States)), Melanie Bell(Ionis Pharmaceuticals (United States))
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