Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model
Heather Gray‐Edwards(UMass Memorial Health Care), Douglas R. Martin(Auburn University), Nouha Salibi(Siemens Healthcare (United States)), Thomas S. Denney(Auburn University), Allison M. Bradbury(Nationwide Children's Hospital), Brandon L. Brunson(Auburn University), Yvonne L. Latour(National Institute of Neurological Disorders and Stroke), Nancy R. Cox(Auburn University), Jean M. Johnston(National Institutes of Health), Peter W. Christopherson(Auburn University), Cynthia J. Tifft(Children's National), Debra S. Regier(Children's National), Miguel Sena‐Esteves(University of Massachusetts Chan Medical School), Victoria J. McCurdy(Auburn University), Aime K. Johnson(Auburn University), Jamie L. Shirley(Auburn University), Sarah Thomas(National Institutes of Health), Ashley N. Randle(Auburn University), Amanda R. Taylor(Auburn University), Henry J. Baker(Auburn University), Gretchen Golas(National Institutes of Health), Donald C. Sorjonen(Auburn University), Ronald J. Beyers(Auburn University)
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