Targeted gene correction of <i>FKRP</i> by CRISPR/Cas9 restores functional glycosylation of α-dystroglycan in cortical neurons derived from human induced pluripotent stem cells
Beatrice Lana(Queen Mary University of London), Yung‐Yao Lin(Queen Mary University of London), Sandra Louzada(Wellcome Sanger Institute), Derek L. Stemple(Wellcome Sanger Institute), Evangelos Konstantinidis(Uppsala University), Beiyuan Fu(Wellcome Sanger Institute), Jihee Kim(Queen Mary University of London), Francesco Muntoni(Great Ormond Street Hospital), Fengtang Yang(Shandong University of Technology), David Ryan(University College Cork), Pentao Liu(Hong Kong Science and Technology Parks Corporation)
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