A novel humanized mouse model of Huntington disease for preclinical development of therapeutics targeting mutant huntingtin alleles
Amber L. Southwell(University of Central Florida), Michael R. Hayden(Family Research Institute), Hailey Findlay Black(Child and Family Research Institute), Yuanyun Xie(University of British Columbia), Erika B. Villanueva(University of British Columbia), Diepiriye G. Iworima(University of British Columbia), Michael E. Østergaard(Ionis Pharmaceuticals (United States)), Crystal N. Doty(University of British Columbia), Holly Kordasiewicz(University of British Columbia), Jolene Ooi(Agency for Science, Technology and Research), William X. Yang(University of California, Los Angeles), Niels H. Skotte(University of British Columbia), Sabine Waltl(University of British Columbia), Eugenia Petoukhov(University of British Columbia), Daphne Cheung(University of British Columbia), Xiaofeng Gu(University of California, Los Angeles), Mahmoud A. Pouladi(Agency for Science, Technology and Research), Louisa Dal Cengio(Child and Family Research Institute), Punit P. Seth(Ionis Pharmaceuticals (United States)), Chris Kay(University of British Columbia), Ramy Slama(University of British Columbia), Eric E. Swayze(Ionis Pharmaceuticals (United States))
Cited by 36
Related Papers
Huntington disease
|Nature Reviews Disease Primers|2015|1.6k
Mutations in HFE2 cause iron overload in chromosome 1q–linked juvenile hemochromatosis
|Nature Genetics|2003|976
Targeted delivery of antisense oligonucleotides to hepatocytes using triantennary<i>N</i>-acetyl galactosamine improves potency 10-fold in mice
|Nucleic Acids Research|2014|594