482. Local and Systemic Gene Editing in a Mouse Model of Duchenne Muscular Dystrophy
Christopher E. Nelson(Duke University), Charles A. Gersbach(Duke University), Matthew Gemberling(Duke University), Pratiksha I. Thakore(Broad Institute), David G. Ousterout(Profectus Biosciences (United States)), Sarina Madhavan(Duke University), Dongsheng Duan(University of Missouri), Chady H. Hakim(National Center for Advancing Translational Sciences), Xiufang Pan(University of Missouri), Feng Zhang(Broad Institute), Winston X. Yan, Ruth Castellanos(University of North Carolina at Chapel Hill), F. Ann Ran(Harvard University), Aravind Asokan(Duke University)
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