Sickle cell disease: an international survey of results of HLA-identical sibling hematopoietic stem cell transplantation

Éliane Gluckman(European Organisation for Rare Diseases), Barbara Cappelli(Scientific Centre of Monaco), Françoise Bernaudin(Université Paris-Est Créteil), Myriam Labopin(Assistance Publique – Hôpitaux de Paris), Fernanda Volt(European Organisation for Rare Diseases), Jeanette Carreras(Medical College of Wisconsin), Belinda Pinto Simões(Universidade de São Paulo), Alina Ferster(Université Libre de Bruxelles), Sophie Dupont(Cliniques Universitaires Saint-Luc), Josu de la Fuente(Imperial College London), Jean‐Hugues Dalle(Université Paris Cité), Marco Zecca, Mark C. Walters(University of California, San Francisco), Lakshmanan Krishnamurti(Aflac (United States)), Monica Bhatia(Morgan Stanley Children's Hospital), Kathryn Leung(Baylor College of Medicine), Gregory A. Yanik(Children's Hospital of Michigan), Joanne Kurtzberg(Duke Medical Center), Nathalie Dhédin(Hôpital Saint-Louis), Mathieu Kuentz(Université Paris-Est Créteil), Gérard Michel(Aix-Marseille Université), Jane F. Apperley(Hammersmith Hospital), Patrick Lutz(Hôpitaux Universitaires de Strasbourg), Bénédicte Neven(Hôpital Necker-Enfants Malades), Yves Bertrand(Hospices Civils de Lyon), Jean Pierre Vannier(Institute for Research and Innovation in Biomedicine), Mouhab Ayas(King Faisal Specialist Hospital & Research Centre), Marina Cavazzana(Délégation Paris 5), Susanne Matthes‐Martin(St Anna Children's Hospital), Vanderson Rocha(European Organisation for Rare Diseases), Hanadi Rafii El-Ayoubi(European Organisation for Rare Diseases), Chantal Kenzey(European Organisation for Rare Diseases), Peter Bader(Goethe University Frankfurt), Franco Locatelli(University of Pavia), Annalisa Ruggeri(European Organisation for Rare Diseases), Mary Eapen(Medical College of Wisconsin)
Blood
December 14, 2016
Cited by 473Open Access
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Abstract

= .013). Twenty-three patients experienced graft failure, and 70 patients (7%) died, with the most common cause of death being infection. The excellent outcome of a cohort transplanted over the course of 3 decades confirms the role of HLA-identical sibling transplantation for children and adults with SCD.


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