CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells
Daniel P. Dever(Stanford University), Rasmus O. Bak(Stanford University), Andreas Reinisch(Stanford University), Joab Camarena(Stanford University), Gabriel C. Washington(Stanford University), Carmencita E. Nicolas(Stanford University), Mara Pavel-Dinu(Stanford University), Nivi Saxena(Stanford University), Alec B. Wilkens(Stanford University), Sruthi Mantri(Stanford University), Nobuko Uchida(StemCells (United States)), Ayal Hendel(Stanford University), Anupama Narla(Stanford University), Ravindra Majeti(Stanford University), Kenneth I. Weinberg(Stanford University), Matthew H. Porteus(Stanford University)
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