Absence of the Autophagy Adaptor SQSTM1/p62 Causes Childhood-Onset Neurodegeneration with Ataxia, Dystonia, and Gaze Palsy

Tobias B. Haack(Technical University of Munich), Thomas Klopstock(Ludwig-Maximilians-Universität München), Thomas Meitinger(Helmholtz Zentrum München), Arcangela Iuso(Helmholtz Zentrum München), Javier Calvo‐Garrido(Karolinska Institutet), Christopher J. Carroll(St George's, University of London), Pirjo Isohanni(University of Helsinki), Henrik Stranneheim(Karolinska University Hospital), Manju A. Kurian(Great Ormond Street Hospital), Paola Venco(Fondazione IRCCS Istituto Neurologico Carlo Besta), Laura S. Kremer(Helmholtz Zentrum München), Per Svenningsson(Karolinska Institutet), Rita Horváth(University of Cambridge), Valeria Tiranti(Fondazione IRCCS Istituto Neurologico Carlo Besta), Martin Paucar(Karolinska University Hospital), Elisabeth Graf(Helmholtz Zentrum München), Anna Wredenberg(Karolinska University Hospital), Camilla Maffezzini(Karolinska Institutet), Erika Ignatius(University of Helsinki), Holger Prokisch(Helmholtz Zentrum München), Tuula Lönnqvist(University of Helsinki), Göran Brandberg(Falun Hospital), Elke Holinski‐Feder(Garvan Institute of Medical Research), Matteo Gorza(Helmholtz Munich), Anu Suomalainen(University of Helsinki), Martin Dichgans(Munich Cluster for Systems Neurology), Jan Senderek(Friedrich Baur Stiftung), Christoph Freyer(Karolinska University Hospital), Tim M. Strom(Ludwig-Maximilians-Universität München), Monika Hartig(Technical University of Munich), Susan Hayflick(Oregon Health & Science University), Anna Wedell(Karolinska University Hospital), Riccardo Berutti(Helmholtz Zentrum München)
The American Journal of Human Genetics
August 22, 2016
Cited by 121


Related Papers