A New Glucocerebrosidase Chaperone Reduces  -Synuclein and Glycolipid Levels in iPSC-Derived Dopaminergic Neurons from Patients with Gaucher Disease and Parkinsonism

Elma Aflaki(National Institutes of Health), Ellen Sidransky(National Institutes of Health)
Journal of Neuroscience
July 13, 2016
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