Targeted gene editing restores regulated CD40L function in X-linked hyper-IgM syndrome

Nicholas Hubbard(University of Washington), Troy R. Torgerson(Allen Institute for Immunology), Karen Sommer, David Hagin(University of Washington), Hans D. Ochs(Infectious Disease Research Institute), Andrew M. Scharenberg(CTI BioPharma (Italy)), Iram Khan, Courtnee Clough(Cincinnati Children's Hospital Medical Center), Yumei Song, David J. Rawlings(Center for Infectious Disease Research)
Blood
February 23, 2016
10.1182/blood-2015-11-683235
Cited by 140

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