Deconstructing Pompe Disease by Analyzing Single Muscle Fibers: “To See a World in a Grain of Sand…”
Nina Raben(APT Therapeutics (United States)), Paul H. Plötz(National Institutes of Health), Shoichi Takikita(National Institutes of Health), Kanneboyina Nagaraju(Children's National), Priya S. Kishnani(Duke University), Benedikt Schoser(Friedrich Baur Stiftung), Bruno Bembi(University of Udine), Laura Page, Suely Kazue Nagahashi Marie(Universidade de São Paulo), Evelyn Ralston(National Institutes of Health), Yin‐Hsiu Chien(National Taiwan University Hospital), María Gabriela Pittis, Ashley Roberts(National Institutes of Health)
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