Gene Therapy for Pyruvate Dehydrogenase E1α Deficiency Using Recombinant Adeno-Associated Virus 2 (rAAV2) Vectors
Renius Owen(University of Florida Health), Terence R. Flotte(University of Massachusetts Chan Medical School), Thomas J. Conlon(Adelson Foundation), Chandramohan V. Ammini, Douglas S. Kerr(University of Otago), Peter W. Stacpoole(University of Florida), Ronald J. Mandel(University of Florida)
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