Safety, Tolerability, and Pharmacokinetics of SMT C1100, a 2-Arylbenzoxazole Utrophin Modulator, following Single- and Multiple-Dose Administration to Pediatric Patients with Duchenne Muscular Dystrophy
Valeria Ricotti(Solidus Biosciences (United States)), Jonathon M. Tinsley(Mary Lyon Centre at MRC Harwell), Neil Robinson, Imelda Hughes(Manchester University NHS Foundation Trust), Helen Roper(Heart of England NHS Foundation Trust), Gary Layton(University of Geneva), Bina Tejura(Summit (United Kingdom)), Kay E. Davies(University of Oxford), Francesco Muntoni(Great Ormond Street Hospital), Stefan Spinty(Alder Hey Children's NHS Foundation Trust)
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