Congenital disorder of glycosylphosphatidylinositol (GPI)-anchor biosynthesis—The phenotype of two patients with novel mutations in the PIGN and PGAP2 genes

Aleksandra Jezela‐Stanek, Ewa Pronicka(Children's Memorial Health Institute), Justyna Spychalska(Instytut Hematologii i Transfuzjologi), Małgorzata Uhrynowska(Instytut Hematologii i Transfuzjologi), Rafał Płoski(Medical University of Warsaw), Małgorzata Rydzanicz(Medical University of Warsaw), Hanna Mierzewska, Dorota Piekutowska‐Abramczuk(Children's Memorial Health Institute), Elżbieta Ciara(Children's Memorial Health Institute), Abdul Rahim Said, Marta Szwarc-Bronikowska(Children's Memorial Health Institute), Dariusz Rokicki(Children's Memorial Health Institute), Piotr Buda(Children's Memorial Health Institute), Elżbieta Jurkiewicz(Children's Memorial Health Institute), Małgorzata Krajewska‐Walasek(Children's Memorial Health Institute), Ewa Jamroz(Medical University of Silesia), Joanna Trubicka(Children's Memorial Health Institute)
European Journal of Paediatric Neurology
February 4, 2016
Cited by 51


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