Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo

Hao Yin(Massachusetts Institute of Technology), Chun‐Qing Song(University of Massachusetts Chan Medical School), J. Robert Dorkin(Massachusetts Institute of Technology), Lihua Julie Zhu(University of Massachusetts Chan Medical School), Yingxiang Li(Tongji University), Qiongqiong Wu(Massachusetts Institute of Technology), Angela Park(University of Massachusetts Chan Medical School), Junghoon Yang(Massachusetts Institute of Technology), Sneha Suresh(Massachusetts Institute of Technology), Aizhan Bizhanova(University of Massachusetts Chan Medical School), Ankit Gupta(University of Massachusetts Chan Medical School), Mehmet Fatih Bolukbasi(University of Massachusetts Chan Medical School), Stephen C. Walsh(Massachusetts Institute of Technology), Roman L. Bogorad(Massachusetts Institute of Technology), Guangping Gao(University of Massachusetts Chan Medical School), Zhiping Weng(University of Massachusetts Chan Medical School), Yizhou Dong(The Ohio State University), Victor Koteliansky(Skolkovo Institute of Science and Technology), Scot A. Wolfe(University of Massachusetts Chan Medical School), Róbert Langer(Harvard–MIT Division of Health Sciences and Technology), Wen Xue(University of Massachusetts Chan Medical School), Daniel G. Anderson(Harvard–MIT Division of Health Sciences and Technology)
Nature Biotechnology
February 1, 2016
Cited by 869Open Access
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