Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial
Nicola G. Ghazi, Fowzan S. Alkuraya(Alfaisal University), Emad B. Abboud(King Khaled Eye Specialist Hospital), Sanford L. Boye(University of Florida), Thomas J. Conlon(Adelson Foundation), Huimin Cai(University of California San Diego), Sawsan R. Nowilaty(King Khaled Eye Specialist Hospital), Fahad Al Saikhan(King Khaled Eye Specialist Hospital), Abdulrahman Almaghamsi(King Khaled Eye Specialist Hospital), Dilek Çolak(King Faisal Specialist Hospital & Research Centre), Abdulrahman Alhommadi(King Khaled Eye Specialist Hospital), David G. Birch(Retina Foundation of the Southwest), Kirsten Erger(University of Florida), Wen‐Tao Deng(University of Florida), Hassan Al-Dhibi(Alfaisal University), William W. Hauswirth(University of Florida), Douglas Vollrath(Stanford University), Kang Zhang(Chinese Academy of Sciences), Wen‐qiu Wang(Shanghai Jiao Tong University), Matthew M. LaVail(University of California, San Francisco), Rui Hou(Shanxi Normal University), Hisham Alkuraya(University of California San Diego), Christopher Chung(University of California San Diego)
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