Prophylactic immune modulation in infantile Ρompe disease using low-dose methotrexate induction: A safe, inexpensive, widely accessible, and efficacious strategy
Zoheb B. Kazi(Duke Medical Center), Priya S. Kishnani(Duke Medical Center), Marianne Rohrbach(Ghent University Hospital), Katalyn Scherer(University of Arizona), Seymour Packman(University of California, San Francisco), Jean‐Marc Nuoffer(University Children’s Hospital Bern), Ankit K. Desai(Duke Medical Center), William B. Rizzo, Angelika Erwin(Cleveland Clinic), Alexandra Joseph(Sanofi (United States)), Bradley Troxler(University of Alabama at Birmingham), Clarisa Maxit(Hospital Italiano de Buenos Aires), Alison McVie‐Wylie, Omar Abdul‐Rahman(Cornell University), Susan Richards(MRC Clinical Trials Unit at UCL), David Kronn(New York Medical College), C. Makris(University of Alabama at Birmingham), Diana Ballhausen(University of Lausanne), M.G. Sabbadini(IRCCS Ospedale San Raffaele), James D. Weisfeld‐Adams(University of Colorado Denver)
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