Antisense Masking of an hnRNP A1/A2 Intronic Splicing Silencer Corrects SMN2 Splicing in Transgenic Mice
Yimin Hua(Cold Spring Harbor Laboratory), Timothy A. Vickers(Ionis Pharmaceuticals (United States)), Hazeem L. Okunola(Cold Spring Harbor Laboratory), C. Frank Bennett(Ionis Pharmaceuticals (United States)), Adrian R. Krainer(Cold Spring Harbor Laboratory)
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