Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia
Mariann Grossman(University of Michigan–Ann Arbor), Steven E. Raper(University of Michigan–Ann Arbor), Karen Kozarsky(University of Michigan–Ann Arbor), Evan A. Stein(Cardiovascular Research Center), John F. Engelhardt(University of Michigan–Ann Arbor), David W.M. Muller(University of Michigan–Ann Arbor), Paul J. Lupien(Université Laval), James M. Wilson(University of Michigan–Ann Arbor)
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