Chemical chaperone ameliorates pathological protein aggregation in plectin-deficient muscle

Lilli Winter(Center for Cancer and Blood Disorders), Gerhard Wiche(Max Perutz Labs), Eva Mihailovska(University of Vienna), Ilona Staszewska(University of Vienna), Irmgard Fischer(University of Vienna), Wolfgang H. Goldmann(Friedrich-Alexander-Universität Erlangen-Nürnberg), Rolf Schröder(Friedrich-Alexander-Universität Erlangen-Nürnberg)
Journal of Clinical Investigation
February 2, 2014
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