Suitability Of Nitisinone In Alkaptonuria 1 (SONIA 1): an international, multicentre, randomised, open-label, no-treatment controlled, parallel-group, dose-response study to investigate the effect of once daily nitisinone on 24-h urinary homogentisic acid excretion in patients with alkaptonuria after 4 weeks of treatment

L. Ranganath; Anna M. Milan; Andrew T. Hughes; John Dutton; Richard J. Fitzgerald; Michael Briggs; Helen Bygott; Eftychia Eirini Psarelli; Trevor F. Cox; James A. Gallagher; Jonathan C. Jarvis; Christa van Kan; Anthony K Hall; Dinny Laan; Birgitta Olsson; Johan Szamosi; Mattias Rudebeck; Torbjörn Kullenberg; Arvid Cronlund; Lennart Svensson; Carin Junestrand; Hana Ayoob; Oliver Timmis; Nicolas Sireau; Kim‐Hanh Le Quan Sang; Federica Genovese; Daniela Braconi; Annalisa Santucci; Martina Nemethova; Andrea Zaťková; Judith C. McCaffrey; Peter Christensen; Gordon Ross; Richard Imrich; Jozef Rovenský

doi:10.1136/annrheumdis-2014-206033

Suitability Of Nitisinone In Alkaptonuria 1 (SONIA 1): an international, multicentre, randomised, open-label, no-treatment controlled, parallel-group, dose-response study to investigate the effect of once daily nitisinone on 24-h urinary homogentisic acid excretion in patients with alkaptonuria after 4 weeks of treatment

L. Ranganath(University of Liverpool), Anna M. Milan(Royal Liverpool University Hospital), Andrew T. Hughes(University of Liverpool), John Dutton(University of Liverpool), Richard J. Fitzgerald(Royal Liverpool University Hospital), Michael Briggs(Royal Liverpool University Hospital), Helen Bygott(University of Liverpool), Eftychia Eirini Psarelli(University of Liverpool), Trevor F. Cox(University of Liverpool), James A. Gallagher(University of Liverpool), Jonathan C. Jarvis(Liverpool John Moores University), Christa van Kan(Western Digital (Netherlands)), Anthony K Hall(Western Digital (Netherlands)), Dinny Laan(Western Digital (Netherlands)), Birgitta Olsson(Swedish Orphan Biovitrum (Sweden)), Johan Szamosi(Swedish Orphan Biovitrum (Sweden)), Mattias Rudebeck(Swedish Orphan Biovitrum (Sweden)), Torbjörn Kullenberg(Swedish Orphan Biovitrum (Sweden)), Arvid Cronlund(Swedish Orphan Biovitrum (Sweden)), Lennart Svensson(Swedish Orphan Biovitrum (Sweden)), Carin Junestrand(Swedish Orphan Biovitrum (Sweden)), Hana Ayoob(Alkaptonuria Society), Oliver Timmis(Alkaptonuria Society), Nicolas Sireau(Alkaptonuria Society), Kim‐Hanh Le Quan Sang(Hôpital Necker-Enfants Malades), Federica Genovese(Nordic Bioscience (Denmark)), Daniela Braconi(University of Siena), Annalisa Santucci(University of Siena), Martina Nemethova(Slovak Academy of Sciences), Andrea Zaťková(Slovak Academy of Sciences), Judith C. McCaffrey(Agilent Technologies (Ireland)), Peter Christensen(Agilent Technologies (United Kingdom)), Gordon Ross(Agilent Technologies (United Kingdom)), Richard Imrich(Slovak Academy of Sciences), Jozef Rovenský(National Institute of Rheumatic Diseases)

Annals of the Rheumatic Diseases

December 5, 2014

10.1136/annrheumdis-2014-206033

Cited by 157Open Access

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