Gene Therapy of Canavan Disease: AAV-2 Vector for Neurosurgical Delivery of Aspartoacylase Gene ( <i>ASPA</i> ) to the Human Brain
Christopher G. Janson(Cooper Hospital), Paola Leone(Bambino Gesù Children's Hospital), Jude Samulski(Duke Medical Center), Mark Testaiuti(Cooper Hospital), Andrew Freese(University of North Carolina at Chapel Hill), Olga Goldfarb(University of North Carolina at Chapel Hill), Larisa Liouterman(University of North Carolina at Chapel Hill), Elizabeth Saslow(University of North Carolina at Chapel Hill), Peter J. Hurh(University of North Carolina at Chapel Hill), William Sharrar(University of North Carolina at Chapel Hill), Joan Rupin(University of North Carolina at Chapel Hill), Michael S. Goldberg(Jefferson Einstein Philadelphia Hospital), Edwin H. Kolodny(University of North Carolina at Chapel Hill), Dah-Jyuu Wang(University of North Carolina at Chapel Hill), John C. Haselgrove, Scott McPhee(AskBio (United States)), Ghassem E. Larijani(University of North Carolina at Chapel Hill), Angelique S. Camp(University of North Carolina at Chapel Hill), David Shera(University of North Carolina at Chapel Hill), Larissa T. Bilaniuk(Children's Hospital of Philadelphia)
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