Pathogenesis of ELANE-mutant severe neutropenia revealed by induced pluripotent stem cells

Ramesh C. Nayak(Cincinnati Children's Hospital Medical Center), José A. Cancelas(Harvard University), Theodosia A. Kalfa(Cincinnati Children's Hospital Medical Center), Marshall S. Horwitz(University of Washington), Patrick J. Paddison(Sage Bionetworks), H. Leighton Grimes(Cincinnati Children's Hospital Medical Center), Bruce J. Aronow(Cincinnati Children's Hospital Medical Center), Ashley M. Wellendorf(Laboratoire d’immunologie intégrative du cancer), Lisa Trump(Cincinnati Children's Hospital Medical Center), C. Alexander Valencia(University of North Carolina at Chapel Hill), Kasiani C. Myers(Immune Deficiency Foundation), Parinda A. Mehta(Cincinnati Children's Hospital Medical Center), Carolyn Lutzko(University of Southern California)
Journal of Clinical Investigation
July 19, 2015
Cited by 82


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