Pompe disease diagnosis and management guideline
Priya S. Kishnani(Duke Medical Center), Robert D. Steiner(Oregon Health & Science University), Deeksha Bali(Duke Medical Center), Kenneth I. Berger(New York University), Barry J. Byrne(University of Florida), Laura E. Case(Duke Medical Center), John F. Crowley(Amicus Therapeutics (United Kingdom)), Steven M. Downs(Indiana University Bloomington), R. Rodney Howell(University of Miami), Richard M. Kravitz(Duke Medical Center), Joanne Mackey(Duke Medical Center), Deborah Marsden(Harvard University Press), Anna Maria Martins(Universidade Federal de São Paulo), David S. Millington(Duke Medical Center), Marc Nicolino(Hôpital Debrousse), Gwen O’grady(Duke Medical Center), Marc C. Patterson(Columbia University), David M. Rapoport(New York University), Alfred E. Slonim(Columbia University), Carolyn T. Spencer(University of Florida), Cynthia J. Tifft(Children's National), Michael S. Watson(American College of Medical Genetics)
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